This is an open-label, long-term extension study to investigate the safety, tolerability and efficacy of DISC-1459 in participants with EPP.
Age: 12 years - 66+
Gender: All
We've found 3 total result s for "Protoporphyria Erythropoietic".
This is a Phase 2, multi-center, double-blind, placebo-controlled, parallel group study of bitopertin to evaluate the safety, tolerability, efficacy, and PPIX concentration change in participants with EPP. Participants may roll over to an open label extension portio...
Age: 18 years - 66+
Gender: All
To evaluate the long-term safety and tolerability of oral dersimelagon.
Age: 12 - 75 years
Gender: All